Search Results - gustavo+aguirre

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Gene therapy for Leber congenital amaurosis ciliopathy

AAV-mediated gene therapy approach for the treatment of Leber congenital amaurosis retinopathies resulting from NPHP5 mutations

Published: 10/16/2023

Gene therapy for the treatment of retinal degeneration and vision loss

Recombinant adeno-associated virus (rAAV) expressing the gene for retinitis pigmentosa GTPAse regulation (RPGR) for the functional and structural rescue of photoreceptor cells of the eye as gene therapy for retinal degeneration and vision loss.

Published: 10/16/2023