Search Results - gustavo+aguirre

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Gene Therapy for Leber Congenital Amaurosis Ciliopathy

AAV-mediated gene therapy approach for the treatment of Leber congenital amaurosis retinopathies resulting from NPHP5 mutations

Published: 7/2/2024
Inventor(s):
Gustavo Aguirre, William Beltran, Samuel Jacobson, Artur Cideciyan
Keywords(s):
 
Category(s):
Technology Classifications > Therapeutics

Gene Therapy for the Treatment of Retinal Degeneration and Vision Loss

Recombinant adeno-associated virus (rAAV) expressing the gene for retinitis pigmentosa GTPAse regulation (RPGR) for the functional and structural rescue of photoreceptor cells of the eye as gene therapy for retinal degeneration and vision loss.

Published: 7/8/2024
Inventor(s):
William Beltran, Gustavo Aguirre, Artur Cideciyan, Samuel Jacobson
Keywords(s):
Gene Therapy
Category(s):
Technology Classifications > Animal Health, Technology Classifications > Therapeutics