New compounds identified through high throughput screening which improve mitochondrial function of Friedreich ataxia cells.
Novel derivatives of oleic acid effectively inhibiting ferroptosis that could be used for treatment of Friedreich Ataxia, neurodegenerative diseases, and neuropsychiatric diseases.
shRNA library of 3 million sequences for identification of small-RNA therapeutic candidates, new targets and pathways, as well as conventional chemical-compound drugs in cell-culture disease models.
A novel treatment for rare disease Friedreich ataxia using p38 or MK2 kinase inhibitors