Search Results - tejvir+khurana

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Site-blocking oligos (SBO) upregulate utrophin for treatment of Duchenne Muscular Dystrophy (DMD

Synthetic oligonucleotides blocking natural degradation of utrophin to treat muscular dystrophy.

Published: 6/20/2024
Inventor(s):
Tejvir Khurana
Keywords(s):
Genetic Disorders, Neurodegenerative Diseases, Orphan Disease
Category(s):
Technology Classifications > Therapeutics

Up-regulators of utrophin expression for the treatment of muscular dystrophy

Small molecules targeting utrophin mRNA untranslated regions overcome post-transcriptional repression

Published: 6/20/2024
Inventor(s):
Tejvir Khurana, Donna Huryn
Keywords(s):
Drug Target, Genetic Disorders
Category(s):
Technology Classifications > Therapeutics

Gene therapy for treatment of Duchenne Muscular Dystrophy (DMD)

Duchenne Muscular Dystrophy (DMD) therapy deletes let-7c miRNA binding sites using CRISPR-Cas9 based genome editing and AAV based delivery.

Published: 6/20/2024
Inventor(s):
Tejvir Khurana
Keywords(s):
Gene Therapy
Category(s):
Technology Classifications > Therapeutics

Therapeutic approach for treatment of Duchenne Muscular Dystrophy

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Published: 2/12/2024
Inventor(s):
Tejvir Khurana
Keywords(s):
 
Category(s):
Technology Classifications > Therapeutics