Search Results - gene+therapy

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Strategies for Mitigating Acute Side Effects of Lung-Targeted Nanocarriers

Approaches and Design Techniques to Alleviate Coagulation-Related Acute Side Effects of Lung-Targeted Nanocarriers

Published: 6/26/2024

Silencing of PRLΔE1 expression: a gene-agnostic treatment for retinal degenerations

Viral vector-mediated gene silencing of a novel short retinal isoform of Prolactin promotes photoreceptor survival.

Published: 7/2/2024

Direct and Effective Method To Reverse The Effects of Fragile X Syndrome

A method of treating Fragile X syndrome by correcting the abnormal DNA clusters causing the characteristic symptoms.

Published: 3/8/2024

mRNA Therapeutics for Corneal Endothelium Regeneration

A novel mRNA-based therapy that induces corneal endothelium regeneration to restore vision loss

Published: 6/27/2024

Ionizable Lipid Nanoparticles For In Vivo mRNA Delivery To The Placenta During Pregnancy

Lipid nanoparticles for selective mRNA delivery to the placenta to treat pre-eclampsia, FGR, and other pregnancy-related disorders.

Published: 2/7/2024

Ligand-Tethered Lipid Nanoparticles for Targeted RNA Delivery to Treat Liver Fibrosis

A new class of anisimide-functionalized lipids that enables targeted delivery of lipid nanoparticles (LNPs) to activated fibroblasts in the liver.

Published: 2/7/2024

Versatile virtual reality system for functional vision evaluation

Virtual reality-based system and software for quick, accurate, and reproducible evaluation of functional vision capacity following clinical treatment

Published: 10/16/2023

High Performance CRISPR-Cas12a System for Combinatorial Genetic Manipulation

CRISPR-Cas12a allowing for simultaneous editing of multiple genes in mammalian cells

Published: 1/10/2024
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