Ten candidate serum and synovial protein levels provide early indication of joint impairment in lysosomal storage disorders.
A library of bi-phosphonate ionizable lipids and LNP formulations to facilitate mRNA delivery to the bone microenvironment.
A new class of anisimide-functionalized lipids that enables targeted delivery of lipid nanoparticles (LNPs) to activated fibroblasts in the liver.
Simplified and reproducible two-step differentiation method optimized for efficient differentiation of human-induced pluripotent stem cells into retinal progenitor cells and functional retinal ganglion cells
Improved cartilage repair via injectable modified polymers that target damaged tissues and enhance cellular response